So what is an Orphan drug anyway?
An orphan drug is a medication that is used to treat life threatening rare diseases (an orphan disease), for which no treatment, or no...
So what is an Orphan drug anyway?
Blau by Genotype
Creating a Blau Database
Uveitis and Blau
Thalidomide, Growth and Blau
CRISPR and Blau Syndrome